Rare Diseases
Article
Foundation Fighting Blindness Opens USH2A Natural History Study
Article
CurePSP International Research Symposium to Take Place in San Francisco
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Conan O’Brien to Host Congenital Hyperinsulinism International Event
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Global CMTC/OVM Conference to Take Place in The Netherlands
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Aplastic Anemia and MDS International Foundation Plans Regional Patient/Family Conference
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Alport Syndrome Research Funding Is Awarded
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NORD Outlines Recommendations for Health Care Reform in Letter to Congressional Leadership
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Rare Disease Film Festival Is Planned
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Join the National Organization for Rare Disorders and the University of Massachusetts for Two Upcoming CME-Accredited Events
From the Journals
Eribulin superior to dacarbazine in advanced liposarcoma
Overall survival with eribulin was 15.6 versus 8.4 months with dacarbazine in a phase 3 randomized trial of 452 patients with advanced liposarcoma...
Conference Coverage
VIDEO: Triple therapy study and new recommendations provide guidance on CAPS
MADRID – New data confirm that triple therapy with anticoagulation, corticosteroids, and plasma exchange or intravenous immunoglobulins increases...