Rare Diseases
Conference Coverage
TTP death linked to elevated troponin and neurological signs
GLASGOW – The registry-based study showed that more than 70% of patients who presented with thrombotic thrombocytopenic purpura had neurological...
From the Journals
Don’t delay palliative care for IPF patients
The sharp decline in quality of life in IPF patients is similar to that seen in lung cancer patients, in contrast to the more gradual trend seen...
Conference Coverage
VIDEO: Immunomodulators for inflammatory skin diseases
WASHINGTON - Off-label therapies discussed by Dr. Friedman include dapsone, hydroxychloroquine, and pentoxifylline.
Conference Coverage
BTK inhibitor calms pemphigus vulgaris with low-dose steroids
WASHINGTON – PRN1008 blocks BTK receptors on B cells, thus forestalling the B-cell mediated inflammatory cascade.
Conference Coverage
Lentiviral gene therapy appears effective in X-CGD
HOUSTON – Results from the small study provide a “proof of concept” for the use of gene therapy in X-linked chronic granulomatous disease,...
From the Journals
List of medications linked to drug-induced lupus expands
A new data-mining study adds 42 new drugs.
News
FDA approves caplacizumab for aTTP
The injection is approved in combination with plasma exchange and immunosuppressive therapy for adults with acquired thrombotic thrombocytopenia...
News
Clinical benefits persist 5 years after thymectomy for myasthenia gravis
Patients with generalized nonthymomatous myasthenia gravis who undergo thymectomy may have better long-term clinical outcomes and require less...
Daily News Podcast
Aspirin and Omega-3 fatty acids fail
Flu activity is ‘high’ in nine states.
News
FDA approves ravulizumab for treatment of paroxysmal nocturnal hemoglobinuria
The drug’s novel formulation means that patients can be treated every eight weeks, instead of every two weeks as is the case with the previously...
From the Journals
Check for neuromyelitis optica spectrum disorder in suspect HIV patients