Rare Diseases
From the Journals
Biosimilar-to-biosimilar switches deemed safe and effective, systematic review reveals
While switches between biosimilars of the same reference biologic already occur for biosimilars with indications in different specialties, they do...
From the Journals
Pandemic tied to misdiagnosis of rare pneumonia
Psittacosis, a rare disease, has been underdiagnosed or misdiagnosed during the COVID-19 pandemic.
Latest News
Topical gel for epidermolysis bullosa shows ongoing benefit
Earlier this year, the FDA declined to approve oleogel-S10 for use in EB, even after it extended its review by 3 months to include additional...
From the Journals
Quality of life benefit exaggerated in some cancer studies
News
FDA approves setmelanotide for obesity in Bardet-Biedl syndrome
The FDA cleared setmelanotide (Imcivree) for people age 6 and older with obesity due to a rare genetic disorder.
Guidelines
Myositis guidelines aim to standardize adult and pediatric care
These are the first guidelines on how to manage adult and pediatric patients with idiopathic inflammatory myopathies (IIM).
Opinion
Dodging potholes from cancer care to hospice transitions
The consequences of suboptimal hospice transitions can damage the mental health and well-being of patient and caregiver.
Latest News
New data confirm risk of Guillain-Barré with J&J COVID shot
Nearly all individuals who developed GBS after the Janssen vaccine had facial weakness or paralysis, in addition to weakness and decreased...
Guidelines
New guideline sheds light on diagnosis, treatment of rare GI syndromes
The U.S. Multi-Society Task Force on Colorectal Cancer provides 14 recommendations for the genetic evaluation, surveillance, and treatment of...
Conference Coverage
Dupilumab treats itch and clears lesions in prurigo nodularis patients
There are currently no Food and Drug Administration–approved systemic therapies for PN.
Conference Coverage
Novel isotretinoin ointment for congenital ichthyosis shows promise
“There is currently no FDA-approved drug for congenital ichthyosis,” Dr. Christopher G. Bunick said.