Rare Diseases
Conference Coverage
CDC: Look for early symptoms of acute flaccid myelitis, report suspected cases
The average age of a patient diagnosed with AFM is 5 years
News
New tickborne virus emerges in China
A previously unknown RNA segmented virus was associated with a febrile illness that spread to 86 patients.
News
FDA approves Zolgensma for infantile-onset SMA treatment
Zolgensma is the first gene therapy for the treatment of infantile-onset spinal muscular atrophy in children aged less than 2 years.
Conference Coverage
Neurodevelopmental concerns may emerge later in Zika-exposed infants
BALTIMORE – Some Zika-exposed children showed poorer mobility and social cognitive scores as they approached 18 months even though their fetal...
Conference Coverage
Is pro soccer a risk factor for ALS?
A higher risk of ALS and an earlier age of onset was found among professional soccer players.
Conference Coverage
Use of levoketoconazole improved several clinical features of Cushing’s disease
LOS ANGELES – Patients’ quality of life scores also grew.
News
Don’t delay palliative care for IPF patients
The sharp decline in quality of life in IPF patients is similar to that seen in lung cancer patients, in contrast to the more gradual trend seen...
Conference Coverage
VIDEO: Immunomodulators for inflammatory skin diseases
WASHINGTON - Off-label therapies discussed by Dr. Friedman include dapsone, hydroxychloroquine, and pentoxifylline.
Conference Coverage
BTK inhibitor calms pemphigus vulgaris with low-dose steroids
WASHINGTON – PRN1008 blocks BTK receptors on B cells, thus forestalling the B-cell mediated inflammatory cascade.
News
List of medications linked to drug-induced lupus expands
A new data-mining study adds 42 new drugs.