Rare Diseases
Conference Coverage
Ehlers-Danlos syndrome: Increased IUGR risk reported
LAS VEGAS – Increased risk of antepartum hemorrhage, cervical incompetence were also seen in the national cohort.
News
FDA approves caplacizumab for aTTP
The injection is approved in combination with plasma exchange and immunosuppressive therapy for adults with acquired thrombotic thrombocytopenia...
News
Meta-analysis: IVIG bests anti-D on platelet count in pediatric ITP
But the clinical significance of this finding is unclear because of the lack of data on bleeding symptoms, according to authors of the meta-...
Literature Review
Clinical benefits persist 5 years after thymectomy for myasthenia gravis
Patients with generalized nonthymomatous myasthenia gravis who undergo thymectomy may have better long-term clinical outcomes and require less...
News
AEDs strongly linked to rare serious skin reactions
The highest-risk AEDs were zonisamide, rufinamide, clorazepate, lamotrigine, carbamazepine, and phenytoin.
News
Fever, intestinal symptoms may delay diagnosis of Kawasaki disease in children
News from the FDA/CDC
FDA approves Xyrem to treat children with narcolepsy
The central nervous system depressant was approved for the treatment of cataplexy and excessive daytime sleepiness.
MS Consult
Identifying and Managing MS Relapse
MS relapse can have a significant impact on patients’ short- and long-term function, quality of life, and finances. Here’s what to look for—and...
News
Bertilimumab granted orphan drug status for bullous pemphigoid
A pivotal phase 2/3 trial of bertilimumab will begin next year, according to the company.